Speakers

Lawrence Steinman, M.D.
Professor
Dept. of Neurology and Neurological Sciences
Chair, Interdepartmental Program in Immunology
Beckman Center for Molecular Medicine
Stanford University

"The Long and Winding Road to Antigen Specific Therapy of Autoimmunity"
Dr. Steinman will discuss antigen specific therapy primarily in the context of Multiple Sclerosis clinical trials.

Samia Khoury, M.D.
Associate Professor
Center for Neurologic Diseases
Brigham and Women's Hospital
Harvard Institutes of Medicine

"Immune Intervention in MS From Bench to Bedside"
Multiple sclerosis is an autoimmune disease affecting central nervous system myelin. Myelin antigen-specific autoreactive cells are activated in the periphery then migrate to the central nervous system where they initiate an inflammatory response.

The animal model for the study of MS is experimental autoimmune encephalomyelitis (EAE). EAE can be induced in a number of species by immunization with myelin antigen and adjuvant. Studies in EAE have helped our understanding of the immune response in multiple sclerosis and many therapies available to patients are first tested in EAE. The past decade has provided a rich interaction between the fields of neurology and immunology. This has given rise to improved understanding of the pathogenesis of multiple sclerosis and the development of new therapies that target specific immune pathways. The demyelinating process in multiple sclerosis (MS) involves T-cells, immunoglobulins and complement, but recent evidence shows that cytokines, chemokines, adhesion molecules, metalloproteinases, nitric oxide and oxygen metabolites, all participate in the effector stages of the disease, and can therefore be potential therapeutic targets.

Peter Mannon, M.D.
Mucosal Immunity Section, Laboratory of Host Defense
National Institute of Allergy and Infectious Diseases
National Institutes of Health

"Experimental Immunomodulation in Inflammatory Bowel Diseases"
Gut mucosal immune responses maintain health and can contribute to disease. This talk will review current concepts of mucosal immunity and mechanisms of gut inflammation to highlight strategies for investigational therapeutics. Data from recent and ongoing trials of investigative agents for Crohn's disease, ulcerative colitis, and inflammatory bowel disease complicating immunodeficiency states will be presented to illustrate these points. Opportunities for targeting novel therapies in human inflammatory bowel diseases will be discussed.

Peter Lipsky, M.D.
Chief, Autoimmunity Branch
National Institute of Arthritis and Musculoskeletal and Skin Diseases
National Institutes of Health
Bethesda MD

"B cell Dysfunction in Human Autoimmunity"
Dr. Lipsky will discuss B cell biology and the role of B cells in autoimmune diseases.

Cornelia Weyand, M.D., Ph.D.
David Lowance Professor of Medicine
Director
Lowance Center for Human Immunology
Emory University School of Medicine

T Cell Aging and Autoimmunity
Rheumatoid arthritis (RA) is a quintessential autoimmune disease manifesting with the combination of a systemic inflammatory syndrome and tissue destructive inflammatory lesions in the joints. T cells, B cells, macrophages, and dendritic cells infiltrate into the synovial membranes and form complex lymphoid microstructures, lending stability and persistency to ongoing immune responses. It has been assumed that recognition of autoantigens initiates the disease process. Recent evidence suggests that antigen-nonspecific aspects of T-cell activation may be equally important in breaking tolerance.

The risk to develop rheumatoid arthritis is age-dependent and is highest in postmenopausal women during the 7th and 8th decade of life. With age emerging as the strongest susceptibility factor it is difficult to envisage the underlying defect in RA as an adaptive immune response to antigen. Adaptive immunity degenerates with age, particularly after the age of 40-50 when thymic T cell production becomes minimal. Defective T cell responses in the elderly are considered the major mechanisms leading to immunosenescence, a state of the immune system characterized by impaired responses to vaccines, infections and tumors. Studies in RA patients have shown that the aging process of the immune system is accelerated by 20 to 30 years and have given rise to the model that premature immunosenescence predisposes to autoimmunity.

RA patients accumulate CD4 T cells that have entered the cellular senescence program. T-cell precursors have excessively proliferated; naive T cells have restrictions in clonal burst. Memory CD4 T cells in RA display a number of phenotypic and functional changes that qualify them as proinflammatory cells. Specifically, RA patients have high frequencies of CD4+CD28- T cells in the blood and in the tissue. These CD4+CD28- T cells show de novo expression of immunoregulatory receptors, such as NKG2D and killer immunoglobuline-like receptors (KIR). They utilize KIRs to kill target cells, even in the absence of T-cell receptor triggering. Cross-linking of KIRs enhances IFN-g production. CD4+CD28- T cells also acquire expression of CX3CR1, the receptor for fractalkine. Fractalkine is abundantly produced by synovial fibroblasts. Membrane-anchored fractalkine enhances T-cell adhesion, co-stimulates IFN- production by CD4+CD28- T cells, and provides survival signals for interacting CD4+CD28- T cells. In essence, memory CD4 T cells in RA are characterized by a panel of novel immunoregulatory receptors through which they obtain a multitude of co-stimulatory signals. Ligands for such co-stimulatory molecules are abundant in the synovial microenvironment, creating a unique niche for senescent CD4+CD28- T cells. Environmental cues different from antigens, such as KIR-binding ligands and fractalkine, can modulate T-cell activation in the lesion and determine outcome of immune responses in this tissue site.

In summary, aged T cells are functionally distinct from young T cells and are characterized by the expression of regulatory receptors driving their activation in the peripheral tissue. This process provides a mechanistic link between accelerated immunosenescence and chronic inflammatory disease in RA.